Company file
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Genethon
Created in 1990 by AFM-TELETHON, Genethon is fully dedicated to the design and development of gene therapy treatments for rare diseases. Its objective is to provide these innovative treatments to patients affected with rare disorders. Genethon is developing therapies for rare neuromuscular diseases, liver diseases and immune system or blood disorders.
Activities
- Research structure
- Cluster or Association
- Analytical Process, Quality assement, Quality Control
- Cleaning
- Quality control
- CMC
- CMC
- Gene Cloning
- Gene augmentation
- Gene inhibition
- Killing Gene
- KI / KO
- (Gene) engineering
- CRISPR activation
- CRISPR interference
- Gene Delivery system
- Lentivirus
- Adeno-Associated Virus (AAV)
- Bioproduction
- Bioproduction
- Scale-Up
- Non-GMP pilot batch
- Ex Vivo & In Vivo Strategy
- Ex Vivo & In Vivo Strategy
- Cell modification
- Gene modification
- Construct introduction
- Cell Expansion
- Bioreacteur
- Purification / extraction
- Purification / extraction
Categories
Expertise
Genetical therapy